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dc.contributor | Universitat de Barcelona |
---|---|
dc.contributor.author | Canals Montferrer, Isaac |
dc.contributor.author | Benetó, Noelia |
dc.contributor.author | Cozar, Mónica |
dc.contributor.author | Vilageliu i Arqués, Lluïsa |
dc.contributor.author | Grinberg Vaisman, Daniel Raúl |
dc.date | 2016-02-24T16:48:50Z |
dc.date | 2016-02-24T16:48:50Z |
dc.date | 2015 |
dc.date | 2016-02-24T16:48:55Z |
dc.identifier.citation | 2045-2322 |
dc.identifier.citation | 654647 |
dc.identifier.uri | http://hdl.handle.net/2445/95835 |
dc.format | 5 p. |
dc.format | application/pdf |
dc.language.iso | eng |
dc.publisher | Nature Publishing Group |
dc.relation | Reproducció del document publicat a: http://dx.doi.org/10.1038/srep13654 |
dc.relation | Scientific Reports, 2015, vol. 5, p. 13654 |
dc.relation | http://dx.doi.org/10.1038/srep13654 |
dc.rights | cc-by-nc-nd (c) Canals Montferrer et al., 2015 |
dc.rights | info:eu-repo/semantics/openAccess |
dc.rights | http://creativecommons.org/licenses/by-nc-nd/3.0/es |
dc.subject | Malalties hereditàries |
dc.subject | Mutació (Biologia) |
dc.subject | Genètica molecular humana |
dc.subject | Malalties neurodegeneratives |
dc.subject | Terapèutica |
dc.subject | Genetic diseases |
dc.subject | Mutation (Biology) |
dc.subject | Human molecular genetics |
dc.subject | Neurodegenerative diseases |
dc.subject | Therapeutics |
dc.title | EXTL2 and EXTL3 inhibition with siRNAs as a promising substrate reduction therapy for Sanfilippo C syndrome |
dc.type | info:eu-repo/semantics/article |
dc.type | info:eu-repo/semantics/publishedVersion |
dc.description.abstract |